My wife and I are proud Wolverines and aunt and uncle to a boy who is living with Duchenne Muscular Dystrophy, the leading genetic killer of children. A drug that is currently in clinical trials has stopped the progression of this previously incurable disease in all trial users. However, this drug only addresses one of the genetic mutations that cause DMD.
The petition linked below asks the FDA to approve this drug on an accelerated timeline (normal approval takes four years). Accelerated Approval will help get this drug - and variants of it that help boys with different genetic mutations, like our nephew - to the kids who need it to be available now. For our nephew and thousands of other boys, this could be the difference between life and death.
This petition is part of a larger campaign you can read about here.
Sign the Petition.
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